Deramiocel heart-derived cellular therapy in advanced Duchenne muscular dystrophy (HOPE-3): a phase 3, randomised, double-blind, placebo-controlled trial

By afschroeder • July 30, 2026

McDonald CM, Villa C, Soslow JH, Maharry K, Hogan N, Binks M, Berth KC, Elliott KA, Taylor M, Hor KN, Signorovich J, Henricson EK, Phan HC, Apkon S, Ghosh PS, Tian C, Veerapandiyan A, Ramos-Platt L, Gambetta K, Bernes SM, Varadhachary AS, Iannaccone ST, Laverty CG, Perlman SJ, Bass NE, Mosher K, Butterfield RJ, Mathews KD, Scharf RJ, Smith EC, Emerson JA, Mercuri E, Awadalla MS, Marbán L, Marbán E; HOPE-3 Investigators. Deramiocel heart-derived cellular therapy in advanced Duchenne muscular dystrophy (HOPE-3): a phase 3, randomised, double-blind, placebo-controlled trial. Lancet. 2026 Jul 29:S0140-6736(26)01385-1. doi: 10.1016/S0140-6736(26)01385-1. Epub ahead of print. PMID: 42526472.

Tags: Cardiology/Epi, Cedars Sinai DoM, Publications

Understanding Cardiac Anatomy and Imaging to Improve Safety of Procedures: The Right Ventricular Outflow Tract, Part 1

Miyazaki Y, Rimmer M, Hanna P, Park YM, Miyazaki K, Yamagami S, Shivkumar K, Mori S. Understanding Cardiac Anatomy and Imaging to Improve Safety of[...]

National Midterm Outcomes of Ex-Vivo Heart Perfusion in Heart Transplantation

Song J, Cho PD, Zappacosta H, White JP, McKay S, Daniel M, Abramov A, Girish A, Telesca D, Husain M, Ardehali A. National Midterm Outcomes[...]

Development of a Primary Care Cardio-Kidney Risk Navigator for Clinical Decision Support

Gluckman TJ, Birkeland K, Bhatt A, Budoff MJ, Danna SC, Desai NR, Norfolk E, Elbedewe A, Kiernan G, Pachpor R, Hirsch J. Development of a[...]