Clinical Outcomes of Lentiviral Vector Gene Therapy for Sickle Cell Disease

By afschroeder • April 22, 2026

Prueksapraopong C, Fernandes A, Campo Fernandez B, Roy S, Hollis RP, Habtemariam B, Pellin D, Ceoldo G, Lin TY, Dang TT, Cornetta K, Romero Z, Blazar BR, Shah AJ, Moore TB, Sehl M, Schiller GJ, Kohn DB. Clinical Outcomes of Lentiviral Vector Gene Therapy for Sickle Cell Disease. Blood Adv. 2026 Apr 20:bloodadvances.2026019869. doi: 10.1182/bloodadvances.2026019869. Epub ahead of print. PMID: 42008008.

Tags: Hematology/Oncology, Publications

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