Emerging Therapies for Sickle Cell Disease: From Symptom Management to Curative Gene Therapy

By afschroeder • November 25, 2025

Duesberg MS, Schiller G. Emerging Therapies for Sickle Cell Disease: From Symptom Management to Curative Gene Therapy. Cureus. 2025 Oct 21;17(10):e95112. doi: 10.7759/cureus.95112. PMID: 41281092; PMCID: PMC12635507.

Tags: crispr-cas9-mediated gene editing, Gene therapy, Hematology/Oncology, hemoglobinopathies, Lentiviral vectors, Publications, sickle cell disease

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