Anakinra in Sanfilippo syndrome: a phase 1/2 trial

Polgreen LE, Chen AH, Pak Y, Luzzi A, Morales Garval A, Acevedo J, Bitan G, Iacovino M, O'Neill C, Eisengart JB. Anakinra in Sanfilippo syndrome: a phase 1/2 trial. Nat Med. 2024 Jun 21. doi: 10.1038/s41591-024-03079-3. Epub ahead of print. PMID: 38907160.


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